OrphanDev was originally a platform dedicated to the specificities of clinical trials in rare diseases.
2005
*
1st Rare Diseases National Plan
Creation of OrphanDev by Dr Joëlle Micallef
pharmacologist and medical manager of the CIC CPCET (Centre for Clinical Pharmacology and Therapeutic Evaluations) of the Timone Hospital in Marseille. Hospital Practitioner in Clinical Pharmacology at the University of Aix Marseille since 2002, she carries out numerous institutional or industrial clinical trials at the CIC. For more than 10 years, she was specifically involved in clinical trials in rare diseases. She was notably the principal investigator of the first clinical trial carried out in patients with Charcot-Marie-Tooth disease type 1A (CMT1A), a clinical trial conducted on 180 patients (Micallef et al, Lancet Neurology 2009). The experience acquired through this trial and others that followed led her to create OrphanDev, a platform dedicated to the specificities of clinical trials in rare diseases.
2009
2014
Since 2014, OrphanDev has been coordinated by Professor Olivier Blin, Head of the Clinical Pharmacology and Pharmacovigilance Department, CHU Timone in Marseille
2020
FCRIN Labeling
2021
Network in its new setup
